Building on our expertise in rare pediatric and adult liver diseases.
Our scientific foundation is rooted in our deep knowledge of bile acid biology. Where research is limited and therapeutic options absent, our teams work urgently to develop novel medicines for children and adults who cannot wait.LEARN MORE
Among our core objectives is to advance scientific research for the benefit of patient care and reducing disease burden. We look to lead and support evidence generation to improve patient outcomes and impact of treatment.LEARN MORE
In the rapidly changing world of drug development, we work to anticipate changes and develop innovative approaches to meeting our goals. We are pursuing commercial partnerships for long-term value with market leading, in-country companies globally whose expertise in particular therapeutic areas is synergistic with our science and product pipeline.